
06/17/2025
Replay the second panel of the 2025 UK Forum "Advances In Individualised Medicine: Are Breakthrough Therapies For Ultra Rare Diseases Within Reach?: https://youtu.be/kQSbWmMPqH0?feature=shared
Chair: Dame June Raine, Former Chief Executive Officer, Medicines and Healthcare products Regulatory Agency
Speakers:
Prof. Matthew Wood, Professor of Neuroscience, Deputy Head Medical Sciences Division (Innovation), University of Oxford, Director and Chief Scientific Officer Oxford-Harrington Rare Disease Centre, Adjunct Professor of Medicine, Case Western Reserve University School of Medicine
Dr. Gregory Friberg, Chief Research & Development Officer, BioMarin Pharmaceutical
Dr. Janet Woodcock, Former Director of the Center for Drug Evaluation and Research and Principal Deputy Commissioner of the U.S. Food and Drug Administration
Dame Sue Hill, CSO for England, Senior Responsible Officer for Genomics in the NHS
Avril Daly, President of EURORDIS
PANEL 2: ADVANCES IN INDIVIDUALISED MEDICINE:ARE BREAKTHROUGH THERAPIES FOR ULTRA RARE DISEASES WITHIN REACH?Chair: Dame June Raine, Former Chief Executive O...